Aug 7, 2021
CRISPR Stops Rare Genetic Disease In Groundbreaking Human Trial
Posted by Genevieve Klien in categories: biotech/medical, genetics
Gene-editing technique CRISPR may deliver new treatments for genetic diseases—and it’s already being tested on patients.
17:22 minutes.
In one of the first clinical applications of the technique, last month researchers reported in the New England Journal of Medicine that CRISPR had stopped a genetic disease called amyloidosis, which occurs when an abnormal protein accumulates in your organs. They’re not the only group moving toward using CRISPR on humans; recently, the FDA approved a human clinical trial that will use the technique to edit genes responsible for sickle cell disease.