Toggle light / dark theme

A CRISPR-based mitochondrial gene therapy tool derived by engineering guide RNAs

Wang et al. systematically analyzed mitochondria-localized lncRNAs to reveal that RBP-motif recognition drives RNA mitochondrial translocation, leading to the engineering of an RNA mitochondrial targeting sequence (RMTS). Fusing RMTS with sgRNA promotes sgRNA mitochondrial entry, establishing a CRISPR-based mitochondrial DNA editing system that ameliorates heteroplasmic mtDNA mutation diseases.

Leave a Comment

Lifeboat Foundation respects your privacy! Your email address will not be published.

/* */