Science and Technology: Gene Therapy apparently Cure Blindness in Children.
S eye, very early in life, to treat a severe form of the condition.‘.
An experimental trial of gene therapy has helped four toddlers — born with one of the most severe forms of childhood blindness — gain “life-changing improvements” to their sight, according to doctors at Moorfields Eye Hospital in London.
The rare genetic condition means the babies’ vision deteriorated very rapidly from birth.
Before the therapy, they were registered legally blind and only just able to distinguish between dark and light. After the infusion, all parents reported improvements — with some of their young children now able to begin to draw and write.