{"id":232547,"date":"2026-03-04T10:08:23","date_gmt":"2026-03-04T16:08:23","guid":{"rendered":"https:\/\/lifeboat.com\/blog\/2026\/03\/presymptomatic-treatment-of-a-genetic-disease-with-a-small-molecule-drug"},"modified":"2026-03-04T10:08:23","modified_gmt":"2026-03-04T16:08:23","slug":"presymptomatic-treatment-of-a-genetic-disease-with-a-small-molecule-drug","status":"publish","type":"post","link":"https:\/\/lifeboat.com\/blog\/2026\/03\/presymptomatic-treatment-of-a-genetic-disease-with-a-small-molecule-drug","title":{"rendered":"Presymptomatic Treatment of a Genetic Disease with a Small-Molecule Drug"},"content":{"rendered":"<p><a class=\"aligncenter blog-photo\" href=\"https:\/\/lifeboat.com\/blog.images\/presymptomatic-treatment-of-a-genetic-disease-with-a-small-molecule-drug2.jpg\"><\/a><\/p>\n<p>A small-molecule drug proves its mettle in the treatment of spinal muscular atrophy, a disease amenable to intervention at the pre-mRNA level.<\/p>\n","protected":false},"excerpt":{"rendered":"<p>A small-molecule drug proves its mettle in the treatment of spinal muscular atrophy, a disease amenable to intervention at the pre-mRNA level.<\/p>\n","protected":false},"author":662,"featured_media":0,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[11,412],"tags":[],"class_list":["post-232547","post","type-post","status-publish","format-standard","hentry","category-biotech-medical","category-genetics"],"_links":{"self":[{"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/posts\/232547","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/users\/662"}],"replies":[{"embeddable":true,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/comments?post=232547"}],"version-history":[{"count":0,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/posts\/232547\/revisions"}],"wp:attachment":[{"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/media?parent=232547"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/categories?post=232547"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/tags?post=232547"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}