{"id":222601,"date":"2025-09-28T00:03:51","date_gmt":"2025-09-28T05:03:51","guid":{"rendered":"https:\/\/lifeboat.com\/blog\/2025\/09\/huntingtons-progression-slowed-by-experimental-gene-therapy"},"modified":"2025-09-28T00:03:51","modified_gmt":"2025-09-28T05:03:51","slug":"huntingtons-progression-slowed-by-experimental-gene-therapy","status":"publish","type":"post","link":"https:\/\/lifeboat.com\/blog\/2025\/09\/huntingtons-progression-slowed-by-experimental-gene-therapy","title":{"rendered":"Huntington\u2019s progression slowed by experimental gene therapy"},"content":{"rendered":"<p><a class=\"aligncenter blog-photo\" href=\"https:\/\/lifeboat.com\/blog.images\/huntingtons-progression-slowed-by-experimental-gene-therapy2.jpg\"><\/a><\/p>\n<p>Even hearing the phrase \u201cHuntington\u2019s disease\u201d will make a room suddenly somber. So the joy that accompanied a recent announcement of results of an experimental gene therapy for the deadly diseases signaled an unfamiliar sense of hope.<\/p>\n<p>In a small clinical trial, brain injections of a virus that codes for a tiny segment of RNA may have prevented the formation of the rogue proteins that make Huntington\u2019s so devastating. The early results, announced September 24 in a news release, show that over three years, the treatment slowed <a href=\"https:\/\/uniqure.gcs-web.com\/node\/12261\/pdf\" target=\"_blank\" rel=\"noopener\">Huntington\u2019s progression by up to 75 percent<\/a>. While not a cure, the treatment could potentially give people living with Huntington\u2019s disease, who might otherwise face early disability and death, the gift of many more years of life.<\/p>\n","protected":false},"excerpt":{"rendered":"<p>Even hearing the phrase \u201cHuntington\u2019s disease\u201d will make a room suddenly somber. So the joy that accompanied a recent announcement of results of an experimental gene therapy for the deadly diseases signaled an unfamiliar sense of hope. In a small clinical trial, brain injections of a virus that codes for a tiny segment of RNA [\u2026]<\/p>\n","protected":false},"author":511,"featured_media":0,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[11,47],"tags":[],"class_list":["post-222601","post","type-post","status-publish","format-standard","hentry","category-biotech-medical","category-neuroscience"],"_links":{"self":[{"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/posts\/222601","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/users\/511"}],"replies":[{"embeddable":true,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/comments?post=222601"}],"version-history":[{"count":0,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/posts\/222601\/revisions"}],"wp:attachment":[{"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/media?parent=222601"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/categories?post=222601"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/tags?post=222601"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}