{"id":135656,"date":"2022-02-15T01:22:19","date_gmt":"2022-02-15T09:22:19","guid":{"rendered":"https:\/\/lifeboat.com\/blog\/2022\/02\/first-gene-therapy-for-tay-sachs-disease-successfully-given-to-two-children"},"modified":"2022-02-15T01:22:19","modified_gmt":"2022-02-15T09:22:19","slug":"first-gene-therapy-for-tay-sachs-disease-successfully-given-to-two-children","status":"publish","type":"post","link":"https:\/\/lifeboat.com\/blog\/2022\/02\/first-gene-therapy-for-tay-sachs-disease-successfully-given-to-two-children","title":{"rendered":"First gene therapy for Tay-Sachs disease successfully given to two children"},"content":{"rendered":"<p><a class=\"aligncenter blog-photo\" href=\"https:\/\/lifeboat.com\/blog.images\/first-gene-therapy-for-tay-sachs-disease-successfully-given-to-two-children2.jpg\"><\/a><\/p>\n<p>About 1 in 300 people in the general population carry the Tay-Sachs disease gene. Ray Kachatorian\/Stone via Getty ImagesTwo babies have received the first-ever gene therapy for Tay-Sachs disease after over 14 years of development. Tay-Sachs is a severe neurological disease caused by a deficiency in an enzyme called HexA. This enzyme breaks down a fatlike substance that normally exists in very small, harmless amounts in the brain. Without HexA, however, this fatlike substance can accumulate to toxic levels that damage and kill neurons.<\/p>\n","protected":false},"excerpt":{"rendered":"<p>About 1 in 300 people in the general population carry the Tay-Sachs disease gene. Ray Kachatorian\/Stone via Getty ImagesTwo babies have received the first-ever gene therapy for Tay-Sachs disease after over 14 years of development. Tay-Sachs is a severe neurological disease caused by a deficiency in an enzyme called HexA. This enzyme breaks down a [\u2026]<\/p>\n","protected":false},"author":556,"featured_media":0,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[11,47],"tags":[],"class_list":["post-135656","post","type-post","status-publish","format-standard","hentry","category-biotech-medical","category-neuroscience"],"_links":{"self":[{"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/posts\/135656","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/users\/556"}],"replies":[{"embeddable":true,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/comments?post=135656"}],"version-history":[{"count":0,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/posts\/135656\/revisions"}],"wp:attachment":[{"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/media?parent=135656"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/categories?post=135656"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/lifeboat.com\/blog\/wp-json\/wp\/v2\/tags?post=135656"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}